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Material Type:
Artigo
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Long-term outcomes of 176 patients with X-linked hyper-IgM syndrome treated with or without hematopoietic cell transplantation

Maria Teresa de la Morena David Leonard; Troy R Torgerson; Otavio Cabral Marques; Mary Anne Slatter; Asghar Aghamohammadi; Sharat Chandra; Luis Murguia Favela; Francisco A Bonilla; Maria Kanariou; Rongras Damrongwatanasuk; Caroline Y Kuo; Christopher C Dvorak; Isabelle Meyts; Karin Chen; Lisa Kobrynski; Neena Kapoor; Darko Richter; Daniela DiGiovanni; Fatima Dhalla; Evangelia Farmaki; Carsten Speckmann; Teresa Español; Anna YU Shcherbina; Imelda Celine Guerra Hanson; Jiri Litzman; John M Routes; Melanie Wong; Ramsay Fuleihan; Suranjith L Seneviratne; Trudy N Small; Ales Janda; Liliana Bezrodnik; Reinhard Seger; Andrea Gomez Raccio; John David M Edgar; Janet Chou; Jordan Keith Abbott; Joris van Montfrans; Luis Ignacio González Granado; Nancy Bunin; Necil Kutukculer; Paul Gray; Gisela Seminario; Srdjan Pasic; Victor Aquino; Christian Wysocki; Hassan Abolhassani; Morna Dorsey; Charlotte Cunningham Rundles; Alan Paul Knutsen; John William Sleasman; Beatriz Tavares Costa Carvalho; Antonio Condino-Neto; Eyal Grunebaum; Helen Chapel; Hans Dieter Ochs; Alexandra Hult Filipovich; Mort Cowan; Andrew Gennery; Andrew James Cant; Luigi D Notarangelo; Chaim M Roifman

Journal of Allergy and Clinical Immunology v. 139, n. 4, p. 1282-1292, 2017

Philadelphia 2017

Item não circula. Consulte sua biblioteca.(Acessar)

2
Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study
Material Type:
Artigo
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Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study

Barzaghi, Federica ; Amaya Hernandez, Laura Cristina ; Neven, Benedicte ; Ricci, Silvia ; Kucuk, Zeynep Yesim ; Bleesing, Jack J. ; Nademi, Zohreh ; Slatter, Mary Anne ; Ulloa, Erlinda Rose ; Shcherbina, Anna ; Roppelt, Anna ; Worth, Austen ; Silva, Juliana ; Aiuti, Alessandro ; Murguia-Favela, Luis ; Speckmann, Carsten ; Carneiro-Sampaio, Magda ; Fernandes, Juliana Folloni ; Baris, Safa ; Ozen, Ahmet ; Karakoc-Aydiner, Elif ; Kiykim, Ayca ; Schulz, Ansgar ; Steinmann, Sandra ; Notarangelo, Lucia Dora ; Gambineri, Eleonora ; Lionetti, Paolo ; Shearer, William Thomas ; Forbes, Lisa R. ; Martinez, Caridad ; Moshous, Despina ; Blanche, Stephane ; Fisher, Alain ; Ruemmele, Frank M. ; Tissandier, Come ; Ouachee-Chardin, Marie ; Rieux-Laucat, Frédéric ; Cavazzana, Marina ; Qasim, Waseem ; Lucarelli, Barbarella ; Albert, Michael H. ; Kobayashi, Ichiro ; Alonso, Laura ; Diaz De Heredia, Cristina ; Kanegane, Hirokazu ; Lawitschka, Anita ; Seo, Jong Jin ; Gonzalez-Vicent, Marta ; Diaz, Miguel Angel ; Goyal, Rakesh Kumar ; Sauer, Martin G. ; Yesilipek, Akif ; Kim, Minsoo ; Yilmaz-Demirdag, Yesim ; Bhatia, Monica ; Khlevner, Julie ; Richmond Padilla, Erick J. ; Martino, Silvana ; Montin, Davide ; Neth, Olaf ; Molinos-Quintana, Agueda ; Valverde-Fernandez, Justo ; Broides, Arnon ; Pinsk, Vered ; Ballauf, Antje ; Haerynck, Filomeen ; Bordon, Victoria ; Dhooge, Catharina ; Garcia-Lloret, Maria Laura ; Bredius, Robbert G. ; Kałwak, Krzysztof ; Haddad, Elie ; Seidel, Markus Gerhard ; Duckers, Gregor ; Pai, Sung-Yun ; Dvorak, Christopher C. ; Ehl, Stephan ; Locatelli, Franco ; Goldman, Frederick ; Gennery, Andrew Richard ; Cowan, Mort J. ; Roncarolo, Maria-Grazia ; Bacchetta, Rosa

Journal of allergy and clinical immunology, 2018-03, Vol.141 (3), p.1036-1049.e5 [Periódico revisado por pares]

United States: Elsevier Inc

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3
Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study
Material Type:
Artigo
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Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study

Ferrua, Francesca ; Galimberti, Stefania ; Courteille, Virginie ; Slatter, Mary Anne ; Booth, Claire ; Moshous, Despina ; Neven, Benedicte ; Blanche, Stephane ; Cavazzana, Marina ; Laberko, Alexandra ; Shcherbina, Anna ; Balashov, Dmitry ; Soncini, Elena ; Porta, Fulvio ; Al-Mousa, Hamoud ; Al-Saud, Bandar ; Al-Dhekri, Hasan ; Arnaout, Rand ; Formankova, Renata ; Bertrand, Yves ; Lange, Andrzej ; Smart, Joanne ; Wolska-Kusnierz, Beata ; Aquino, Victor M ; Dvorak, Christopher C ; Fasth, Anders ; Fouyssac, Fanny ; Heilmann, Carsten ; Hoenig, Manfred ; Schuetz, Catharina ; Kelecic, Jadranka ; Bredius, Robbert G.M ; Lankester, Arjan C ; Lindemans, Caroline A ; Suarez, Felipe ; Sullivan, Kathleen E ; Albert, Michael H ; Kalwak, Krzysztof ; Barlogis, Vincent ; Bhatia, Monica ; Bordon, Victoria ; Czogala, Wojciech ; Alonso, Laura ; Dogu, Figen ; Gozdzik, Jolanta ; Ikinciogullari, Aydan ; Krivan, Gergely ; Ljungman, Per ; Meyts, Isabelle ; Mustillo, Peter ; Smith, Angela R ; Speckmann, Carsten ; Sundin, Mikael ; Keogh, Steven John ; Shaw, Peter John ; Boelens, Jaap Jan ; Schulz, Ansgar S ; Sedlacek, Petr ; Veys, Paul ; Mahlaoui, Nizar ; Janda, Ales ; Davies, E. Graham ; Fischer, Alain ; Cowan, Morton J ; Gennery, Andrew Richard

JOURNAL OF ALLERGY AND CLINICAL IMMUNOLOGY, 2019-06, Vol.143 (6), p.2238-2253 [Periódico revisado por pares]

MOSBY-ELSEVIER

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4
Long-term follow-up of IPEX syndrome patients after different therapeutic strategies : an international multicenter retrospective study
Material Type:
Artigo
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Long-term follow-up of IPEX syndrome patients after different therapeutic strategies : an international multicenter retrospective study

Barzaghi, Federica ; Hernandez, Laura Cristina Amaya ; Neven, Benedicte ; Ricci, Silvia ; Kucuk, Zeynep Yesim ; Bleesing, Jack J ; Nademi, Zohreh ; Slatter, Mary Anne ; Ulloa, Erlinda Rose ; Shcherbina, Anna ; Roppelt, Anna ; Worth, Austen ; Silva, Juliana ; Aiuti, Alessandro ; Murguia-Favela, Luis ; Speckmann, Carsten ; Carneiro-Sampaio, Magda ; Fernandes, Juliana Folloni ; Baris, Safa ; Ozen, Ahmet ; Karakoc-Aydiner, Elif ; Kiykim, Ayca ; Schulz, Ansgar ; Steinmann, Sandra ; Notarangelo, Lucia Dora ; Gambineri, Eleonora ; Lionetti, Paolo ; Shearer, William Thomas ; Forbes, Lisa R ; Martinez, Caridad ; Moshous, Despina ; Blanche, Stephane ; Fisher, Alain ; Ruemmele, Frank M ; Tissandier, Come ; Ouachee-Chardin, Marie ; Rieux-Laucat, Frederic ; Cavazzana, Marina ; Qasim, Waseem ; Lucarelli, Barbarella ; Albert, Michael H ; Kobayashi, Ichiro ; Alonso, Laura ; De Heredia, Cristina Diaz ; Kanegane, Hirokazu ; Lawitschka, Anita ; Seo, Jong Jin ; Gonzalez-Vicent, Marta ; Diaz, Miguel Angel ; Goyal, Rakesh Kumar ; Sauer, Martin G ; Yesilipek, Akif ; Kim, Minsoo ; Yilmaz-Demirdag, Yesim ; Bhatia, Monica ; Khlevner, Julie ; Padilla, Erick J Richmond ; Martino, Silvana ; Montin, Davide ; Neth, Olaf ; Molinos-Quintana, Agueda ; Valverde-Fernandez, Justo ; Broides, Arnon ; Pinsk, Vered ; Ballauf, Antje ; Haerynck, Filomeen ; Bordon Cueto De Braem, Maria ; Dhooge, Catharina ; Garcia-Lloret, Maria Laura ; Bredius, Robbert G ; Kawak, Krzysztof ; Haddad, Elie ; Seidel, Markus Gerhard ; Duckers, Gregor ; Pai, Sung-Yun ; Dvorak, Christopher C ; Ehl, Stephan ; Locatelli, Franco ; Goldman, Frederick ; Gennery, Andrew Richard ; Cowan, Mort J ; Roncarolo, Maria-Grazia ; Bacchetta, Rosa

2018

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5
Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study
Material Type:
Artigo
Adicionar ao Meu Espaço

Long-term follow-up of IPEX syndrome patients after different therapeutic strategies: An international multicenter retrospective study

Barzaghi, Federica ; Amaya Hernandez, Laura Cristina ; Neven, Benedicte ; Ricci, Silvia ; Kucuk, Zeynep Yesim ; Bleesing, Jack J ; Nademi, Zohreh ; Slatter, Mary Anne ; Ulloa, Erlinda Rose ; Shcherbina, Anna ; Roppelt, Anna ; Worth, Austen ; Silva, Juliana ; Aiuti, Alessandro ; Murguia-Favela, Luis ; Speckmann, Carsten ; Carneiro-Sampaio, Magda ; Fernandes, Juliana Folloni ; Baris, Safa ; Ozen, Ahmet ; Karakoc-Aydiner, Elif ; Kiykim, Ayca ; Schulz, Ansgar ; Steinmann, Sandra ; Notarangelo, Lucia Dora ; Gambineri, Eleonora ; Lionetti, Paolo ; Shearer, William Thomas ; Forbes, Lisa R ; Martinez, Caridad ; Moshous, Despina ; Blanche, Stephane ; Fisher, Alain ; Ruemmele, Frank M ; Tissandier, Come ; Ouachee-Chardin, Marie ; Rieux-Laucat, Frédéric ; Cavazzana, Marina ; Qasim, Waseem ; Lucarelli, Barbarella ; Albert, Michael H ; Kobayashi, Ichiro ; Alonso, Laura ; Diaz De Heredia, Cristina ; Kanegane, Hirokazu ; Lawitschka, Anita ; Seo, Jong Jin ; Gonzalez-Vicent, Marta ; Diaz, Miguel Angel ; Goyal, Rakesh Kumar ; Sauer, Martin G ; Yesilipek, Akif ; Kim, Minsoo ; Yilmaz-Demirdag, Yesim ; Bhatia, Monica ; Khlevner, Julie ; Richmond Padilla, Erick J ; Martino, Silvana ; Montin, Davide ; Neth, Olaf ; Molinos-Quintana, Agueda ; Valverde-Fernandez, Justo ; Broides, Arnon ; Pinsk, Vered ; Ballauf, Antje ; Haerynck, Filomeen ; Bordon, Victoria ; Dhooge, Catharina ; Garcia-Lloret, Maria Laura ; Bredius, Robbert G ; Kałwak, Krzysztof ; Haddad, Elie ; Seidel, Markus Gerhard ; Duckers, Gregor ; Pai, Sung-Yun ; Dvorak, Christopher C ; Ehl, Stephan ; Locatelli, Franco ; Goldman, Frederick ; Gennery, Andrew Richard ; Cowan, Mort J ; Roncarolo, Maria-Grazia ; Bacchetta, Rosa ; Primary Immune Deficiency Treatment Consortium (PIDTC) and the Inborn Errors Working Party (IEWP) of the European Society for Blood and Marrow Transplantation (EBMT)

The Journal of allergy and clinical immunology, 2018-03, Vol.141 (3), p.1036-1049.e5

eScholarship, University of California

Sem texto completo

6
Hematopoietic Cell Transplant for CD40 Ligand Deficiency—Comparing Busulfan Versus Treosulfan
Material Type:
Artigo
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Hematopoietic Cell Transplant for CD40 Ligand Deficiency—Comparing Busulfan Versus Treosulfan

Carruthers, Vicky-Anne ; Lum, Su Han ; Flood, Terence ; Slatter, Mary A. ; Gennery, Andrew R.

Journal of clinical immunology, 2022-04, Vol.42 (3), p.703-705 [Periódico revisado por pares]

New York: Springer US

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7
Long-term outcome following hematopoietic stem-cell transplantation in Wiskott-Aldrich syndrome: collaborative study of the European Society for Immunodeficiencies and European Group for Blood and Marrow Transplantation
Material Type:
Artigo
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Long-term outcome following hematopoietic stem-cell transplantation in Wiskott-Aldrich syndrome: collaborative study of the European Society for Immunodeficiencies and European Group for Blood and Marrow Transplantation

Ozsahin, Hulya ; Cavazzana-Calvo, Marina ; Notarangelo, Luigi D. ; Schulz, Ansgar ; Thrasher, Adrian J. ; Mazzolari, Evelina ; Slatter, Mary A. ; Le Deist, Francoise ; Blanche, Stephane ; Veys, Paul ; Fasth, Anders ; Bredius, Robbert ; Sedlacek, Petr ; Wulffraat, Nico ; Ortega, Juan ; Heilmann, Carsten ; O’Meara, Anne ; Wachowiak, Jacek ; Kalwak, Krzysztof ; Matthes-Martin, Susanne ; Gungor, Tayfun ; Ikinciogullari, Aydan ; Landais, Paul ; Cant, Andrew J. ; Friedrich, Wilhelm ; Fischer, Alain

Blood, 2008-01, Vol.111 (1), p.439-445 [Periódico revisado por pares]

Washington, DC: Elsevier Inc

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8
Monogenic early-onset lymphoproliferation and autoimmunity: Natural history of STAT3 gain-of-function syndrome
Material Type:
Artigo
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Monogenic early-onset lymphoproliferation and autoimmunity: Natural history of STAT3 gain-of-function syndrome

Leiding, Jennifer W. ; Vogel, Tiphanie P. ; Smith, Madison R. ; Carisey, Alexandre ; Vargas-Hernández, Alexander ; Silva-Carmona, Manuel ; Neven, Bénédicte ; Ronan Leahy, Timothy ; Taskinen, Mervi ; Kostyuchenko, Larysa ; Scherbina, Anna ; Bauer, Cindy S. ; Giovannini-Chami, Lisa ; Romberg, Neil ; Prince, Benjamin T. ; Bohnsack, John ; Pachlopnik Schmid, Jana ; Bahna, Sami ; Brothers, Shannon ; Chan, Alice Y. ; Chandrakasan, Shanmuganathan ; Christiansen, Mette ; Cole, Theresa ; Desai, Mukesh M. ; Gottrand, Frédéric ; Grimbacher, Bodo ; Hoffman, Hal M. ; Guerrerio, Anthony L. ; Kainulainen, Leena ; Lawrence, Monica G. ; Martelius, Timi ; Neth, Olaf ; Lugo Reyes, Saúl Oswaldo ; Russell, Mark A. ; Schejter, Yael ; Skevofilax, Effie ; Suan, Daniel ; Velasco, Helena ; Walkovich, Kelly ; Aleshkevich, Svetlana ; Allende, Luis M. ; Atschekzei, Faranaz ; Aygunes, Utku ; Barlogis, Vincent ; Belko, John ; Bezrodnik, Liliana ; Biebl, Ariane ; Caldirola, Maria Soledad ; Castelle, Martin ; Cokugras, Haluk ; Cox, Fionnuala ; Dalgic, Buket ; ASH Dalm, Virgil ; Dujovny, Tal ; Eken, Ahmet ; Fabre, Alexandre ; Fischer, Alain ; Hannibal, Mark ; Huppert, Laura ; Karakoc-Aydiner, Elif ; Pac Kisaarslan, Ayşenur ; Kiykim, Ayca ; Klocperk, Adam ; Kuzmenko, Natalia ; Lianou, Dimitra ; Lorenz, Myriam Ricarda ; Manson, Ania ; Marega, Lia Furlaneto ; Nolan, David ; Norlin, Anna-Carin ; Oleastro, Matias ; Ozcan, Alper ; Picard, Capucine ; Polychronopoulou, Sophia ; Quesada, Juan Francisco ; Randall, Katrina L. ; Resin, Geraldine ; Rodina, Yulia ; Rohrlich, Pierre ; Sachs, Johnathan ; Sakovich, Inga ; Santarlas, Christopher ; Scheffler Mendoza, Selma C. ; Schwarz, Klaus ; Sediva, Anna ; Slatter, Mary ; Sleasman, John ; Suratannon, Narissara ; Tanita, Kay ; Travis, Stephen ; Tsinti, Maria ; Unal, Ekrem ; Urdinez, Luciano ; Vazquez-Gomez, Felisa ; Weiss, Mitchell J. ; Zhang, Yu ; Seppänen, Mikko R.J. ; Sogkas, Georgios ; Milner, Joshua D. ; Forbes Satter, Lisa R.

Journal of allergy and clinical immunology, 2023-04, Vol.151 (4), p.1081-1095 [Periódico revisado por pares]

United States: Elsevier Inc

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9
Long-term immune reconstitution after anti-CD52–treated or anti-CD34–treated hematopoietic stem cell transplantation for severe T-lymphocyte immunodeficiency
Material Type:
Artigo
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Long-term immune reconstitution after anti-CD52–treated or anti-CD34–treated hematopoietic stem cell transplantation for severe T-lymphocyte immunodeficiency

Slatter, Mary A., MD ; Brigham, Kenneth, MPhil ; Dickinson, Anne M., PhD ; Harvey, Helen L., BSc ; Barge, Dawn, PhD ; Jackson, Antony, BSc ; Bown, Nicholas, PhD ; Flood, Terence J., MD ; Cant, Andrew J., MD ; Abinun, Mario, MD ; Gennery, Andrew R., MD

Journal of allergy and clinical immunology, 2008-02, Vol.121 (2), p.361-367 [Periódico revisado por pares]

New York, NY: Mosby, Inc

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10
Association of busulfan exposure and outcomes after HCT for patients with an inborn error of immunity
Material Type:
Artigo
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Association of busulfan exposure and outcomes after HCT for patients with an inborn error of immunity

Bognàr, Tim ; Garcia-Rosa, Moises ; Lalmohamed, Arief ; Güngör, Tayfun ; Hauri-Hohl, Mathias ; Prockop, Susan ; Oram, Layne ; Pai, Sung-Yun ; Brooks, Jordan ; Savic, Rada M. ; Dvorak, Christopher C. ; Long-Boyle, Janel R. ; Krajinovic, Maja ; Bittencourt, Henrique ; Teyssier, Anne-Charlotte ; Théorêt, Yves ; Martinez, Cary ; Egberts, Toine C. G. ; Morales, Erin ; Slatter, Mary ; Cuvelier, Geoffrey D. E. ; Chiesa, Robert ; Wynn, Robert F. ; Coussons, Mary ; Cicalese, Maria P. ; Ansari, Marc ; Long, Susan E. ; Ebens, Christen L. ; Lust, Hannah ; Chaudhury, Sonali ; Nath, Christa E. ; Shaw, Peter J. ; Keogh, Steven J. ; van der Stoep, M. Y. Eileen C. ; Bredius, Robbert ; Lindemans, Caroline A. ; Boelens, Jaap-Jan ; Bartelink, Imke H.

Blood advances, 2024-07 [Periódico revisado por pares]

Elsevier Inc

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Deste Autor:

  1. Meyts, I
  2. Wysocki, C
  3. Notarangelo, L
  4. Kapoor, N
  5. Dhalla, F

Buscando em bases de dados remotas. Favor aguardar.