Correction of feline lipoprotein lipase deficiency with adeno-associated virus serotype 1-mediated gene transfer of the lipoprotein lipase S447X beneficial mutation
ROSS, Colin J. D ; TWISK, Jaap ; KUIVENHOVEN, Jan Albert ; MEULENBERG, Janneke M ; HAYDEN, Michael R ; BARKER, Andrew C ; FUDAN MIAO ; VERBART, Dennis ; RIP, Jaap ; GODBEY, Tamara ; DIJKHUIZEN, Paul ; HERMENS, Wim T. J. M. C ; KASTELEIN, John J. P
Human gene therapy, 2006-05, Vol.17 (5), p.487-499 [Periódico revisado por pares]Larchmont, NY: Liebert
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