L‐leucine improves anemia and growth in patients with transfusion‐dependent Diamond‐Blackfan anemia: Results from a multicenter pilot phase I/II study from the Diamond‐Blackfan Anemia Registry
Vlachos, Adrianna ; Atsidaftos, Evangelia ; Lababidi, Mohammad Lutfi ; Muir, Ellen ; Rogers, Zora R. ; Alhushki, Waseem ; Bernstein, Jonathan ; Glader, Bertil ; Gruner, Barbara ; Hartung, Helge ; Knoll, Christine ; Loew, Thomas ; Nalepa, Grzegorz ; Narla, Anupama ; Panigrahi, Arun R. ; Sieff, Colin A. ; Walkovich, Kelly ; Farrar, Jason E. ; Lipton, Jeffrey M.
Pediatric blood & cancer, 2020-12, Vol.67 (12), p.e28748-n/a [Periódico revisado por pares]United States: Wiley Subscription Services, Inc
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