Exon-skipping antisense oligonucleotides for cystic fibrosis therapy

Kim, Young Jin ; Sivetz, Nicole ; Layne, Jessica ; Voss, Dillon M ; Yang, Lucia ; Zhang, Qian ; Krainer, Adrian R

Proceedings of the National Academy of Sciences - PNAS, 2022-01, Vol.119 (3) [Periódico revisado por pares]

United States: National Academy of Sciences

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