Gene correction of human induced pluripotent stem cells repairs the cellular phenotype in pulmonary alveolar proteinosis
Lachmann, Nico ; Happle, Christine ; Ackermann, Mania ; Lüttge, Doreen ; Wetzke, Martin ; Merkert, Sylvia ; Hetzel, Miriam ; Kensah, George ; Jara-Avaca, Monica ; Mucci, Adele ; Skuljec, Jelena ; Dittrich, Anna-Maria ; Pfaff, Nils ; Brennig, Sebastian ; Schambach, Axel ; Steinemann, Doris ; Göhring, Gudrun ; Cantz, Tobias ; Martin, Ulrich ; Schwerk, Nicolaus ; Hansen, Gesine ; Moritz, Thomas
American journal of respiratory and critical care medicine, 2014-01, Vol.189 (2), p.167-182 [Periódico revisado por pares]United States: American Thoracic Society
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