Eteplirsen for the treatment of Duchenne muscular dystrophy
Mendell, Jerry R. ; Rodino-Klapac, Louise R. ; Sahenk, Zarife ; Roush, Kandice ; Bird, Loren ; Lowes, Linda P. ; Alfano, Lindsay ; Gomez, Ann Maria ; Lewis, Sarah ; Kota, Janaiah ; Malik, Vinod ; Shontz, Kim ; Walker, Christopher M. ; Flanigan, Kevin M. ; Corridore, Marco ; Kean, John R. ; Allen, Hugh D. ; Shilling, Chris ; Melia, Kathleen R. ; Sazani, Peter ; Saoud, Jay B. ; Kaye, Edward M.
Annals of neurology, 2013-11, Vol.74 (5), p.637-647 [Periódico revisado por pares]United States: Blackwell Publishing Ltd
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