Cerebrospinal Fluid Calbindin D Concentration as a Biomarker of Cerebellar Disease Progression in Niemann-Pick Type C1 Disease
Bradbury, Allison ; Bagel, Jessica ; Sampson, Maureen ; Farhat, Nicole ; Ding, Wenge ; Swain, Gary ; Prociuk, Maria ; O'Donnell, Patricia ; Drobatz, Kenneth ; Gurda, Brittney ; Wassif, Christopher ; Remaley, Alan ; Porter, Forbes ; Vite, Charles
The Journal of pharmacology and experimental therapeutics, 2016-08, Vol.358 (2), p.254-261 [Periódico revisado por pares]United States: The American Society for Pharmacology and Experimental Therapeutics
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