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Material Type: Artigo
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Systemic Treatment of Fabry Disease Using a Novel AAV9 Vector Expressing α-Galactosidase ABiferi, Maria Grazia ; Cohen-Tannoudji, Mathilde ; García-Silva, Andrea ; Souto-Rodríguez, Olga ; Viéitez-González, Irene ; San-Millán-Tejado, Beatriz ; Fernández-Carrera, Andrea ; Pérez-Márquez, Tania ; Teijeira-Bautista, Susana ; Barrera, Soraya ; Domínguez, Vanesa ; Marais, Thibaut ; González-Fernández, África ; Barkats, Martine ; Ortolano, SaidaMolecular therapy. Methods & clinical development, 2021-03, Vol.20, p.1-17 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |