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1
Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy
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Artigo
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Eplontersen for Hereditary Transthyretin Amyloidosis With Polyneuropathy

Coelho, Teresa ; Marques, Jr, Wilson ; Dasgupta, Noel R ; Chao, Chi-Chao ; Parman, Yesim ; França, Jr, Marcondes Cavalcante ; Guo, Yuh-Cherng ; Wixner, Jonas ; Ro, Long-Sun ; Calandra, Cristian R ; Kowacs, Pedro A ; Berk, John L ; Obici, Laura ; Barroso, Fabio A ; Weiler, Markus ; Conceição, Isabel ; Jung, Shiangtung W ; Buchele, Gustavo ; Brambatti, Michela ; Chen, Jersey ; Hughes, Steven G ; Schneider, Eugene ; Viney, Nicholas J ; Masri, Ahmad ; Gertz, Morie R ; Ando, Yukio ; Gillmore, Julian D ; Khella, Sami ; Dyck, P James B ; Waddington Cruz, Márcia

JAMA : the journal of the American Medical Association, 2023-10, Vol.330 (15), p.1448-1458 [Periódico revisado por pares]

United States: American Medical Association

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2
Worldwide experience of homozygous familial hypercholesterolaemia: retrospective cohort study
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Artigo
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Worldwide experience of homozygous familial hypercholesterolaemia: retrospective cohort study

Tromp, Tycho R ; Hartgers, Merel L ; Hovingh, G Kees ; Soran, Handrean ; Freiberger, Tomas ; Bertolini, Stefano ; Harada-Shiba, Mariko ; Cuchel, Marina ; Tromp, Tycho R. ; Hartgers, Merel L. ; Vallejo-Vaz, Antonio J. ; Soran, Handrean ; Bertolini, Stefano A. ; Pang, Jing ; Watts, Gerald F. ; Stulnig, Thomas M. ; Descamps, Olivier S. ; Rymen, Daisy ; Witters, Peter ; Brunham, Liam R. ; Genest, Jacques ; Ruel, Isabelle ; Wang, Luya ; Reiner, Željko ; Ceska, Richard ; Dvorakova, Jana ; Dlouhy, Lubomir ; Horak, Pavel ; Soska, Vladimir ; Tichy, Lukas ; Urbanek, Robin ; Vaverkova, Helena ; Vrablik, Michal ; Zemek, Stanislav ; Reda, Ashraf ; Béliard, Sophie ; Bruckert, Eric ; Elisaf, Moses S. ; Cohen, Hofit ; Elis, Avishay ; Hussein, Osama ; Setia, Nitika ; Verma, Ishwar C. ; Alareedh, Mohammed D. ; Rhadi, Sabah H. ; Shaghee, Foaad K. ; Arca, Marcello ; Averna, Maurizio ; Bucci, Marco ; Buonuomo, Paola S. ; Calabrò, Paolo ; Casula, Manuela ; Cefalù, Angelo B. ; D'Addato, Sergio ; Di Costanzo, Alessia ; Fasano, Tommaso ; Gazzotti, Marta ; Rabacchi, Claudio ; Ripoli, Carlo ; Sbrana, Francesco ; Tarugi, Patrizia ; Trenti, Chiara ; Hori, Mika ; Ayesh, Mahmoud H. ; Azar, Sami T. ; Bitar, Fadi F. ; Madriz, Ramón ; Cupido, Arjen J. ; Reijman, M. Doortje ; Roeters-van Lennep, Jeanine E. ; Wiegman, Albert ; Zuurbier, Linda ; Sadiq, Fouzia ; Chlebus, Krzysztof ; Susekov, Andrey V. ; Charng, Min-Ji ; Aktan, Melih ; Altunkeser, Bulent B. ; Demircioglu, Sinan ; Kose, Melis ; Ilhan, Osman ; Kayikcioglu, Meral ; Kuku, Irfan ; Kurtoglu, Erdal ; Okutan, Harika ; Ozcebe, Osman I. ; Pekkolay, Zafer ; Yenercag, Mustafa ; Yilmaz Yasar, Hamiyet ; Lyons, Alexander R.M. ; Nguyen, Christina ; Alieva, Rano ; Shek, Aleksandr ; Do, Doan-Loi ; Kim, Ngoc-Thanh ; Le, Hong-An ; Truong, Thanh-Huong ; Blom, Dirk J. ; Raal, Frederick J. ; Cuchel, Marina

The Lancet (British edition), 2022-02, Vol.399 (10326), p.719-728 [Periódico revisado por pares]

England: Elsevier Ltd

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3
Mechanical power in pediatric acute respiratory distress syndrome: a PARDIE study
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Artigo
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Mechanical power in pediatric acute respiratory distress syndrome: a PARDIE study

Bhalla, Anoopindar K ; Klein, Margaret J ; Modesto I Alapont, Vicent ; Emeriaud, Guillaume ; Kneyber, Martin C J ; Medina, Alberto ; Cruces, Pablo ; Diaz, Franco ; Takeuchi, Muneyuki ; Maddux, Aline B ; Mourani, Peter M ; Camilo, Cristina ; White, Benjamin R ; Yehya, Nadir ; Pappachan, John ; Di Nardo, Matteo ; Shein, Steven ; Newth, Christopher ; Khemani, Robinder

Critical care (London, England), 2022-01, Vol.26 (1), p.2-2, Article 2 [Periódico revisado por pares]

England: BioMed Central Ltd

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4
Initial antimicrobial management of sepsis
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Artigo
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Initial antimicrobial management of sepsis

Niederman, Michael S ; Baron, Rebecca M ; Bouadma, Lila ; Calandra, Thierry ; Daneman, Nick ; DeWaele, Jan ; Kollef, Marin H ; Lipman, Jeffrey ; Nair, Girish B

Critical care (London, England), 2021-08, Vol.25 (1), p.307-307, Article 307 [Periódico revisado por pares]

England: BioMed Central Ltd

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5
Initial antimicrobial management of sepsis
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Artigo
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Initial antimicrobial management of sepsis

Niederman, Michael S ; Baron, Rebecca M ; Bouadma, Lila ; Calandra, Thierry ; Daneman, Nick ; De Waele, Jan ; Kollef, Marin H ; Lipman, Jeffrey ; Nair, Girish B

2021

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6
Risk factors for candidemia: a prospective matched case-control study
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Artigo
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Risk factors for candidemia: a prospective matched case-control study

Poissy, Julien ; Damonti, Lauro ; Bignon, Anne ; Khanna, Nina ; Von Kietzell, Matthias ; Boggian, Katia ; Neofytos, Dionysios ; Vuotto, Fanny ; Coiteux, Valérie ; Artru, Florent ; Zimmerli, Stephan ; Pagani, Jean-Luc ; Calandra, Thierry ; Sendid, Boualem ; Poulain, Daniel ; van Delden, Christian ; Lamoth, Frédéric ; Marchetti, Oscar ; Bochud, Pierre-Yves

Critical care (London, England), 2020-03, Vol.24 (1), p.109-109, Article 109 [Periódico revisado por pares]

England: BioMed Central Ltd

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7
Evidence for Updating the Core Domain Set of Outcome Measures for Juvenile Idiopathic Arthritis: Report from a Special Interest Group at OMERACT 2016
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Artigo
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Evidence for Updating the Core Domain Set of Outcome Measures for Juvenile Idiopathic Arthritis: Report from a Special Interest Group at OMERACT 2016

Morgan, Esi M ; Riebschleger, Meredith P ; Horonjeff, Jennifer ; Consolaro, Alessandro ; Munro, Jane E ; Thornhill, Susan ; Beukelman, Timothy ; Brunner, Hermine I ; Creek, Emily L ; Harris, Julia G ; Horton, Daniel B ; Lovell, Daniel J ; Mannion, Melissa L ; Olson, Judyann C ; Rahimi, Homaira ; Gallo, Maria Chiara ; Calandra, Serena ; Ravelli, Angelo ; Ringold, Sarah ; Shenoi, Susan ; Stinson, Jennifer ; Toupin-April, Karine ; Strand, Vibeke ; Bingham, 3rd, Clifton O

Journal of rheumatology, 2017-12, Vol.44 (12), p.1884-1888 [Periódico revisado por pares]

Canada

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8
A genome-wide association study in multiple system atrophy
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Artigo
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A genome-wide association study in multiple system atrophy

Sailer, Anna ; Scholz, Sonja W ; Nalls, Michael A ; Schulte, Claudia ; Federoff, Monica ; Price, T Ryan ; Lees, Andrew ; Ross, Owen A ; Dickson, Dennis W ; Mok, Kin ; Mencacci, Niccolo E ; Schottlaender, Lucia ; Chelban, Viorica ; Ling, Helen ; OʼSullivan, Sean S ; Wood, Nicholas W ; Traynor, Bryan J ; Ferrucci, Luigi ; Federoff, Howard J ; Mhyre, Timothy R ; Morris, Huw R ; Deuschl, Günther ; Quinn, Niall ; Widner, Hakan ; Albanese, Alberto ; Infante, Jon ; Bhatia, Kailash P ; Poewe, Werner ; Oertel, Wolfgang ; Höglinger, Günter U ; Wüllner, Ullrich ; Goldwurm, Stefano ; Pellecchia, Maria Teresa ; Ferreira, Joaquim ; Tolosa, Eduardo ; Bloem, Bastiaan R ; Rascol, Olivier ; Meissner, Wassilios G ; Hardy, John A ; Revesz, Tamas ; Holton, Janice L ; Gasser, Thomas ; Wenning, Gregor K ; Singleton, Andrew B ; Houlden, Henry

Neurology, 2016-10, Vol.87 (15), p.1591-1598 [Periódico revisado por pares]

United States: American Academy of Neurology

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9
Holmes tremor: Clinical description, lesion localization, and treatment in a series of 29 cases
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Artigo
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Holmes tremor: Clinical description, lesion localization, and treatment in a series of 29 cases

Raina, Gabriela B ; Cersosimo, Maria G ; Folgar, Silvia S ; Giugni, Juan C ; Calandra, Cristian ; Paviolo, Juan P ; Tkachuk, Veronica A ; Zuñiga Ramirez, Carlos ; Tschopp, Andrea L ; Calvo, Daniela S ; Pellene, Luis A ; Uribe Roca, Marcela C ; Velez, Miriam ; Giannaula, Rolando J ; Fernandez Pardal, Manuel M ; Micheli, Federico E

Neurology, 2016-03, Vol.86 (10), p.931-938 [Periódico revisado por pares]

United States: American Academy of Neurology

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10
Cyclooxygenase and prostaglandins in somatic cell populations of the testis
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Artigo
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Cyclooxygenase and prostaglandins in somatic cell populations of the testis

Frungieri, Mónica B ; Calandra, Ricardo S ; Mayerhofer, Artur ; Matzkin, María E

Reproduction (Cambridge, England), 2015-04, Vol.149 (4), p.R169-R180 [Periódico revisado por pares]

England: Bioscientifica Ltd

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