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Micro-dystrophin expression levels result in reduced mdx pathologyRodino-Klapac, Louise R ; Janssen, Paul ML ; Montgomery, Chrystal L ; Coley, Brian D ; Chicoine, Louis G ; K Reed Clark ; Mendell, Jerry Rfigshare 2011Texto completo disponível |
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A translational approach for limb vascular delivery of the micro-dystrophin gene without high volume or high pressure for treatment of Duchenne muscular dystrophy-4Rodino-Klapac, Louise R ; Janssen, Paul ML ; Montgomery, Chrystal L ; Coley, Brian D ; Chicoine, Louis G ; K Reed Clark ; Mendell, Jerry Rfigshare 2011Texto completo disponível |