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Material Type: Artigo
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Serum matrix metalloproteinase-9 (MMP-9) as a biomarker for monitoring disease progression in Duchenne muscular dystrophy (DMD)Nadarajah, V.D ; van Putten, M ; Chaouch, A ; Garrood, P ; Straub, V ; Lochmüller, H ; Ginjaar, H.B ; Aartsma-Rus, A.M ; van Ommen, G.J.B ; den Dunnen, J.T ; t Hoen, P.A.CNeuromuscular disorders : NMD, 2011-08, Vol.21 (8), p.569-578 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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Quantitative MRI and strength measurements in the assessment of muscle quality in Duchenne muscular dystrophyWokke, B.H ; van den Bergen, J.C ; Versluis, M.J ; Niks, E.H ; Milles, J ; Webb, A.G ; van Zwet, E.W ; Aartsma-Rus, A ; Verschuuren, J.J ; Kan, H.ENeuromuscular disorders : NMD, 2014-05, Vol.24 (5), p.409-416 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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Muscle biopsies in clinical trials for Duchenne muscular dystrophy – Patients’ and caregivers’ perspectiveVerhaart, Ingrid E.C. ; Johnson, Alex ; Thakrar, Sejal ; Vroom, Elizabeth ; De Angelis, Fernanda ; Muntoni, Francesco ; Aartsma-Rus, Annemieke M. ; Niks, Erik H.Neuromuscular disorders : NMD, 2019-08, Vol.29 (8), p.576-584 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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P260 The vitamin B3 analogue nicotinamide riboside has only very minor effects on reducing muscle damage in mdx miceStan, T. ; vd Vijver, D. ; Verhaart, I. ; Aartsma-Rus, A.Neuromuscular disorders : NMD, 2023-10, Vol.33, p.S148-S148 [Periódico revisado por pares]Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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194th ENMC international workshop. 3rd ENMC workshop on exon skipping: Towards clinical application of antisense-mediated exon skipping for Duchenne muscular dystrophy 8–10 December 2012, Naarden, The NetherlandsAartsma-Rus, Annemieke ; Muntoni, FrancescoNeuromuscular disorders : NMD, 2013-11, Vol.23 (11), p.934-944 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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Meeting report of the “Regulatory Exchange Matters” session at the 5th International TREAT-NMD ConferenceAartsma-Rus, Annemieke ; Mercuri, Eugenio ; Vroom, Elizabeth ; Balabanov, PavelNeuromuscular disorders : NMD, 2018-07, Vol.28 (7), p.619-623 [Periódico revisado por pares]Texto completo disponível |
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Material Type: Artigo
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The therapeutic potential of soluble activin type IIB receptor treatment in a limb girdle muscular dystrophy type 2D mouse modelAlqallaf, Ali ; Engelbeen, Sarah ; Palo, Angela ; Cutrupi, Federico ; Tanganyika-de Winter, Christa ; Plomp, Jaap ; Vaiyapuri, Sakthivel ; Aartsma-Rus, Annemieke ; Patel, Ketan ; van Putten, MaaikeNeuromuscular disorders : NMD, 2022-05, Vol.32 (5), p.419-435 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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Comparison of skeletal muscle pathology and motor function of dystrophin and utrophin deficient mouse strainsvan Putten, Maaike ; Kumar, Darshan ; Hulsker, Margriet ; Hoogaars, Willem M.H ; Plomp, Jaap J ; van Opstal, Annemarieke ; van Iterson, Maarten ; Admiraal, Peter ; van Ommen, Gert-Jan B ; t Hoen, Peter A.C ; Aartsma-Rus, AnnemiekeNeuromuscular disorders : NMD, 2012-05, Vol.22 (5), p.406-417 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |
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Material Type: Artigo
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DMD - BRAINVerhaeg, M. ; Adamzek, K. ; Vijver, D. Van De ; Putker, K. ; Engelbeen, S. ; Suidgeest, E. ; Overzier, M. ; van der Weerd, L. ; Aartsma-Rus, A. ; Putten, M.Neuromuscular disorders : NMD, 2021-10, Vol.31, p.S90 [Periódico revisado por pares]Texto completo disponível |
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Material Type: Artigo
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Report on the workshop: Meaningful outcome measures for Duchenne muscular dystrophy, London, UK, 30–31 January 2017Straub, Volker ; Mercuri, Eugenio ; Aartsma-Rus, Annemieke ; Athanasiou, Dimitrios ; Balabanov, Pavel ; Buccella, Filippo ; Caizergues, Didier ; Carlier, Pierre ; Crossley, Emily ; Connolly, Anne M. ; Duong, Tina ; Fischer, Dirk ; Furlong, Pat ; Goemans, Nathalie ; de Groot, Imelda ; Guglieri, Michela ; Henricson, Erik ; Johnson, Alex ; Kan, Hermien E. ; Mayhew, Anna ; Mazzone, Elena ; McDonald, Craig M. ; Mercuri, Eugenio ; Muntoni, Francesco ; Niks, Erik H. ; Servais, Laurent ; Turner, Cathy ; Voit, Thomas ; Vroom, Elizabeth ; Walter, GlennNeuromuscular disorders : NMD, 2018-08, Vol.28 (8), p.690-701 [Periódico revisado por pares]England: Elsevier B.VTexto completo disponível |