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Long-term outcomes of 176 patients with X-linked hyper-IgM syndrome treated with or without hematopoietic cell transplantation

Maria Teresa de la Morena David Leonard; Troy R Torgerson; Otavio Cabral Marques; Mary Anne Slatter; Asghar Aghamohammadi; Sharat Chandra; Luis Murguia Favela; Francisco A Bonilla; Maria Kanariou; Rongras Damrongwatanasuk; Caroline Y Kuo; Christopher C Dvorak; Isabelle Meyts; Karin Chen; Lisa Kobrynski; Neena Kapoor; Darko Richter; Daniela DiGiovanni; Fatima Dhalla; Evangelia Farmaki; Carsten Speckmann; Teresa Español; Anna YU Shcherbina; Imelda Celine Guerra Hanson; Jiri Litzman; John M Routes; Melanie Wong; Ramsay Fuleihan; Suranjith L Seneviratne; Trudy N Small; Ales Janda; Liliana Bezrodnik; Reinhard Seger; Andrea Gomez Raccio; John David M Edgar; Janet Chou; Jordan Keith Abbott; Joris van Montfrans; Luis Ignacio González Granado; Nancy Bunin; Necil Kutukculer; Paul Gray; Gisela Seminario; Srdjan Pasic; Victor Aquino; Christian Wysocki; Hassan Abolhassani; Morna Dorsey; Charlotte Cunningham Rundles; Alan Paul Knutsen; John William Sleasman; Beatriz Tavares Costa Carvalho; Antonio Condino-Neto; Eyal Grunebaum; Helen Chapel; Hans Dieter Ochs; Alexandra Hult Filipovich; Mort Cowan; Andrew Gennery; Andrew James Cant; Luigi D Notarangelo; Chaim M Roifman

Journal of Allergy and Clinical Immunology v. 139, n. 4, p. 1282-1292, 2017

Philadelphia 2017

Localização: ICB - Inst. Ciências Biomédicas    (PC ICB BMI SEP 2017 )(Acessar)

2
Long term outcomes of 176 patients with X-linked hyper IgM syndrome treated with or without hematopoietic cell transplantation
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Artigo
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Long term outcomes of 176 patients with X-linked hyper IgM syndrome treated with or without hematopoietic cell transplantation

de la Morena, M Teresa ; Leonard, David ; Torgerson, Troy R ; Cabral-Marques, Otavio ; Slatter, Mary ; Aghamohammadi, Asghar ; Chandra, Sharat ; Murguia-Favela, Luis ; Bonilla, Francisco ; Kanariou, Maria ; Damrongwatanasuk, Rongras ; Kuo, Caroline Y ; Dvorak, Christopher C ; Meyts, Isabelle ; Chen, Karin ; Kobrynski, Lisa ; Kapoor, Neena ; Richter, Darko ; DiGiovanni, Daniela ; Dhalla, Fatima ; Farmaki, Evangelia ; Speckmann, Carsten ; Espanol, Teresa ; Shcherbina, Anna ; Hanson, Celine ; Litzman, Jiri ; Routes, John ; Wong, Melanie ; Fuleihan, Ramsay ; Seneviratne, Suranjith L ; Small, Trudy N ; Janda, Ales ; Bezrodnik, Liliana ; Seger, Reinhard ; Raccio, Andrea Gomez ; Edgar, J David M ; Chou, Janet ; Abbott, Jordan K ; van Montfrans, Joris ; Gonzalez-Granado, Luis Ignacio ; Bunin, Nancy ; Kutukculer, Necil ; Gray, Paul ; Seminario, Gisela ; Pasic, Srdjan ; Aquino, Victor ; Wysocki, Christian ; Abolhassani, Hassan ; Grunebaum, Eyal ; Dorsey, Morna ; Costa Carvalho, Beatriz Tavares ; Condino-Neto, Antonio ; Cunningham-Rundles, Charlotte ; Knutsen, Alan P ; Sleasman, John ; Chapel, Helen ; Ochs, Hans D ; Filipovich, Alexandra ; Cowan, Mort ; Gennery, Andrew ; Cant, Andrew ; Notarangelo, Luigi D ; Roifman, Chaim

Journal of Allergy and Clinical Immunology, 2017-04, Vol.139 (4), p.1282-1292 [Periódico revisado por pares]

Elsevier

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3
Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study
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Artigo
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Hematopoietic stem cell transplantation for CD40 ligand deficiency: Results from an EBMT/ESID-IEWP-SCETIDE-PIDTC study

Ferrua, F. ; Galimberti, S. ; Courteille, V. ; Slatter, M.A. ; Booth, C. ; Moshous, D. ; Neven, B. ; Blanche, S. ; Cavazzana, M. ; Laberko, A. ; Shcherbina, A. ; Balashov, D. ; Soncini, E. ; Porta, F. ; Al-Mousa, H. ; Al-Saud, B. ; Al-Dhekri, H. ; Arnaout, R. ; Formankova, R. ; Bertrand, Y. ; Lange, A. ; Smart, J. ; Wolska-Kusnierz, B. ; Aquino, V.M. ; Dvorak, C.C. ; Fasth, A. ; Fouyssac, F. ; Heilmann, C. ; Hoenig, M. ; Schuetz, C. ; Kelecic, J. ; Bredius, R.G.M. ; Lankester, A.C. ; Lindemans, C.A. ; Suarez, F. ; Sullivan, K.E. ; Albert, M.H. ; Kalwak, K. ; Barlogis, V. ; Bhatia, M. ; Bordon, V. ; Czogala, W. ; Alonso, L. ; Dogu, F. ; Gozdzik, J. ; Ikinciogullari, A. ; Krivan, G. ; Ljungman, P. ; Meyts, I. ; Mustillo, P. ; Smith, A.R. ; Speckmann, C. ; Sundin, M. ; Keogh, S.J. ; Shaw, P.J. ; Boelens, J.J. ; Schulz, A.S. ; Sedlacek, P. ; Veys, P. ; Mahlaoui, N. ; Janda, A. ; Davies, E.G. ; Fischer, A. ; Cowan, M.J. ; Gennery, A.R.

Journal of Allergy and Clinical Immunology, 2019-06, Vol.143 (6), p.2238-2253

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