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Material Type: Artigo
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Regulatory news: Nulibry (fosdenopterin) approved to reduce the risk of mortality in patients with molybdenum cofactor deficiency type A: FDA approval summaryFarrell, Sheila ; Karp, Jacqueline ; Hager, Rebecca ; Wang, Yan ; Adeniyi, Oluseyi ; Wang, Jie ; Li, Liang ; Ma, Lian ; Peretz, Jackye ; Summan, Mukesh ; Kong, Nicolas ; White, Michael ; Pacanowski, Michael ; Price, Dionne ; Filie, Jane ; Donohue, Kathleen ; Joffe, HyltonJournal of inherited metabolic disease, 2021-09, Vol.44 (5), p.1085-1087 [Periódico revisado por pares]Hoboken, USA: John Wiley & Sons, IncTexto completo disponível |
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Material Type: Artigo
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A molecular basis underpinning the T cell receptor heterogeneity of mucosal-associated invariant T cellsEckle, Sidonia B G ; Birkinshaw, Richard W ; Kostenko, Lyudmila ; Corbett, Alexandra J ; McWilliam, Hamish E G ; Reantragoon, Rangsima ; Chen, Zhenjun ; Gherardin, Nicholas A ; Beddoe, Travis ; Liu, Ligong ; Patel, Onisha ; Meehan, Bronwyn ; Fairlie, David P ; Villadangos, Jose A ; Godfrey, Dale I ; Kjer-Nielsen, Lars ; McCluskey, James ; Rossjohn, JamieThe Journal of experimental medicine, 2014-07, Vol.211 (8), p.1585-1600 [Periódico revisado por pares]United States: The Rockefeller University PressTexto completo disponível |
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Material Type: Artigo
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Mitigation of Radiation-Induced Lung and Heart Injuries in Mice by Oral Sepiapterin after IrradiationRabender, Christopher S. ; Mezzaroma, Eleonora ; Yakovlev, Vasily A. ; Mauro, Adolfo G. ; Bonaventura, Aldo ; Abbate, Antonio ; Mikkelsen, Ross B.Radiation research, 2021-05, Vol.195 (5), p.463-473 [Periódico revisado por pares]United States: Radiation Research SocietyTexto completo disponível |
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Material Type: Artigo
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Multiple Routes to Color Convergence in a Radiation of Neotropical Poison FrogsTwomey, Evan ; Melo-Sampaio, Paulo ; Schulte, Lisa M ; Bossuyt, Franky ; Brown, Jason L ; Castroviejo-Fisher, Santiago Bell, RaynaSystematic biology, 2023-12, Vol.72 (6), p.1247-1261 [Periódico revisado por pares]US: Oxford University PressTexto completo disponível |
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Material Type: Artigo
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Lipophilic Decyl Chain–Pterin Conjugates with Sensitizer PropertiesVignoni, Mariana ; Walalawela, Niluksha ; Bonesi, Sergio M ; Greer, Alexander ; Thomas, Andrés HMolecular pharmaceutics, 2018-03, Vol.15 (3), p.798-807 [Periódico revisado por pares]United States: American Chemical SocietyTexto completo disponível |
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Material Type: Artigo
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Phase I clinical evaluation of CNSA-001 (sepiapterin), a novel pharmacological treatment for phenylketonuria and tetrahydrobiopterin deficiencies, in healthy volunteersSmith, Neil ; Longo, Nicola ; Levert, Keith ; Hyland, Keith ; Blau, NenadMolecular genetics and metabolism, 2019-04, Vol.126 (4), p.406-412 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Folate Biosynthesis, Turnover, and Transport in PlantsHanson, Andrew D ; Gregory, Jesse F. IIIAnnual review of plant biology, 2011-01, Vol.62 (1), p.105-125 [Periódico revisado por pares]United States: Annual Reviews IncTexto completo disponível |
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Material Type: Artigo
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Diverse Aromatic Metabolites in the Solitary Tunicate Cnemidocarpa ireneMiyako, Kei ; Yasuno, Yoko ; Shinada, Tetsuro ; Fujita, Masaki J ; Sakai, RyuichiJournal of natural products (Washington, D.C.), 2020-10, Vol.83 (10), p.3156-3165 [Periódico revisado por pares]United States: American Chemical Society and American Society of PharmacognosyTexto completo disponível |
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Material Type: Artigo
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PTC923 (sepiapterin) lowers elevated blood phenylalanine in subjects with phenylketonuria: a phase 2 randomized, multi-center, three-period crossover, open-label, active controlled, all-comers studyBratkovic, Drago ; Margvelashvili, Lali ; Tchan, Michel C. ; Nisbet, Janelle ; Smith, NeilMetabolism, clinical and experimental, 2022-03, Vol.128, p.155116, Article 155116 [Periódico revisado por pares]United States: Elsevier IncTexto completo disponível |
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Material Type: Artigo
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Bisubstrate inhibitors of 6-hydroxymethyl-7,8-dihydropterin pyrophosphokinase: Transition state analogs for high affinity bindingShi, Genbin ; Shaw, Gary X. ; Zhu, Fengxia ; Tarasov, Sergey G. ; Ji, XinhuaBioorganic & medicinal chemistry, 2021-01, Vol.29, p.115847-115847, Article 115847 [Periódico revisado por pares]England: Elsevier LtdTexto completo disponível |