Eteplirsen for the treatment of Duchenne muscular dystrophy

Mendell, Jerry R. ; Rodino-Klapac, Louise R. ; Sahenk, Zarife ; Roush, Kandice ; Bird, Loren ; Lowes, Linda P. ; Alfano, Lindsay ; Gomez, Ann Maria ; Lewis, Sarah ; Kota, Janaiah ; Malik, Vinod ; Shontz, Kim ; Walker, Christopher M. ; Flanigan, Kevin M. ; Corridore, Marco ; Kean, John R. ; Allen, Hugh D. ; Shilling, Chris ; Melia, Kathleen R. ; Sazani, Peter ; Saoud, Jay B. ; Kaye, Edward M.

United States: Blackwell Publishing Ltd

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Long-term enhancement of skeletal muscle mass and strength by single gene administration of myostatin inhibitors

Haidet, Amanda M ; Rizo, Liza ; Handy, Chalonda ; Umapathi, Priya ; Eagle, Amy ; Shilling, Chris ; Boue, Daniel ; Martin, Paul T ; Sahenk, Zarife ; Mendell, Jerry R ; Kaspar, Brian K

United States: National Academy of Sciences

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Dystrophin Immunity in Duchenne's Muscular Dystrophy

Mendell, Jerry R ; Campbell, Katherine ; Rodino-Klapac, Louise ; Sahenk, Zarife ; Shilling, Chris ; Lewis, Sarah ; Bowles, Dawn ; Gray, Steven ; Li, Chengwen ; Li, Juan ; Galloway, Gloria ; Malik, Vinod ; Coley, Brian ; Clark, K. Reed ; Xiao, Xiao ; Samulski, R. Jude ; Samulski, Jade ; McPhee, Scott W ; Walker, Christopher M

Waltham, MA: Massachusetts Medical Society

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Sustained alpha-sarcoglycan gene expression after gene transfer in limb-girdle muscular dystrophy, type 2D

Mendell, Jerry R. ; Rodino-Klapac, Louise R. ; Rosales, Xiomara Q. ; Coley, Brian D. ; Galloway, Gloria ; Lewis, Sarah ; Malik, Vinod ; Shilling, Chris ; Byrne, Barry J. ; Conlon, Thomas ; Campbell, Katherine J. ; Bremer, William G. ; Taylor, Laura E. ; Flanigan, Kevin M. ; Gastier-Foster, Julie M. ; Astbury, Caroline ; Kota, Janaiah ; Sahenk, Zarife ; Walker, Christopher M. ; Clark, K. Reed

Hoboken: Wiley Subscription Services, Inc., A Wiley Company

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Sustained alpha-sarcoglycan gene expression following gene transfer in LGMD2D

Mendell, Jerry R. ; Rodino-Klapac, Louise R. ; Rosales, Xiomara Q. ; Coley, Brian D. ; Galloway, Gloria ; Lewis, Sarah ; Malik, Vinod ; Shilling, Chris ; Byrne, Barry J. ; Conlon, Thomas ; Campbell, Katherine J. ; Bremer, William G. ; Taylor, Laura E. ; Flanigan, Kevin M. ; Kota, Janaiah ; Sahenk, Zarife ; Walker, Christopher M. ; Clark, K. Reed

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Dystrophin Immunity in Duchenne's Muscular DystrophyBrief Report

Mendell, Jerry R ; Campbell, Katherine ; Rodino-Klapac, Louise ; Sahenk, Zarife ; Shilling, Chris ; Lewis, Sarah ; Bowles, Dawn ; Gray, Steven ; Li, Chengwen ; Galloway, Gloria ; Malik, Vinod ; Coley, Brian ; Clark, K Reed ; Li, Juan ; Xiao, Xiao ; Samulski, Jade ; McPhee, Scott W ; Samulski, R Jude ; Walker, Christopher M

Boston: Massachusetts Medical Society

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Revertant muscle fibers expressing dystrophin do not tolerize the immune system in Duchenne muscular dystrophy: lessons learned from a Phase I clinical trial (96.9)

Campbell, Katherine ; Rodino-Klapac, Louise ; Sahenk, Zarife ; Shilling, Chris ; Lewis, Sarah ; Bowles, Dawn ; Gray, Steven ; Li, Chengwen ; Galloway, Gloria ; Malik, Vinod ; Coley, Brian ; Clark, Reed ; Li, Juan ; Xiao, Xiao ; Samulski, Jade ; McPhee, Scott ; Samulski, R.Jude ; Mendell, Jerry ; Walker, Christopher

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914. Recombinant AAV Gene Delivery of Follistatin for Muscle Enhancement in Models of Muscular Dystrophy

Rizo, Liza ; Shilling, Chris ; Haidet, Amanda ; Umapathi Umapathi, Priya ; Sahenk, Zarife ; Mendell, Jerry R. ; Kaspar, Brian K.

Milwaukee: Elsevier Limited

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TrkB and TrkC agonist antibodies improve function, electrophysiologic and pathologic features in TremblerJ mice

Sahenk, Zarife ; Galloway, Gloria ; Edwards, Chris ; Malik, Vinod ; Kaspar, Brian K. ; Eagle, Amy ; Yetter, Brent ; Forgie, Alison ; Tsao, David ; Lin, John C.

Amsterdam: Elsevier Inc

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