Result Number | Material Type | Add to My Shelf Action | Record Details and Options |
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1 |
Material Type: Artigo
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Detailed comparison of retroviral vectors and promoter configurations for stable and high transgene expression in human induced pluripotent stem cellsHoffmann, D ; Schott, J W ; Geis, F K ; Lange, L ; Müller, F-J ; Lenz, D ; Zychlinski, D ; Steinemann, D ; Morgan, M ; Moritz, T ; Schambach, AGene therapy, 2017-05, Vol.24 (5), p.298-307 [Periódico revisado por pares]England: Nature Publishing GroupTexto completo disponível |
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2 |
Material Type: Artigo
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Lentiviral vectors containing an enhancer-less ubiquitously acting chromatin opening element (UCOE) provide highly reproducible and stable transgene expression in hematopoietic cellsZhang, Fang ; Thornhill, Susannah I. ; Howe, Steven J. ; Ulaganathan, Meera ; Schambach, Axel ; Sinclair, Joanna ; Kinnon, Christine ; Gaspar, H. Bobby ; Antoniou, Michael ; Thrasher, Adrian J.Blood, 2007-09, Vol.110 (5), p.1448-1457 [Periódico revisado por pares]Washington, DC: Elsevier IncTexto completo disponível |
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3 |
Material Type: Artigo
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A Modified γ-Retrovirus Vector for X-Linked Severe Combined ImmunodeficiencyHacein-Bey-Abina, Salima ; Pai, Sung-Yun ; Gaspar, H. Bobby ; Armant, Myriam ; Berry, Charles C ; Blanche, Stephane ; Bleesing, Jack ; Blondeau, Johanna ; de Boer, Helen ; Buckland, Karen F ; Caccavelli, Laure ; Cros, Guilhem ; De Oliveira, Satiro ; Fernández, Karen S ; Guo, Dongjing ; Harris, Chad E ; Hopkins, Gregory ; Lehmann, Leslie E ; Lim, Annick ; London, Wendy B ; van der Loo, Johannes C.M ; Malani, Nirav ; Male, Frances ; Malik, Punam ; Marinovic, M. Angélica ; McNicol, Anne-Marie ; Moshous, Despina ; Neven, Benedicte ; Oleastro, Matías ; Picard, Capucine ; Ritz, Jerome ; Rivat, Christine ; Schambach, Axel ; Shaw, Kit L ; Sherman, Eric A ; Silberstein, Leslie E ; Six, Emmanuelle ; Touzot, Fabien ; Tsytsykova, Alla ; Xu-Bayford, Jinhua ; Baum, Christopher ; Bushman, Frederic D ; Fischer, Alain ; Kohn, Donald B ; Filipovich, Alexandra H ; Notarangelo, Luigi D ; Cavazzana, Marina ; Williams, David A ; Thrasher, Adrian JThe New England journal of medicine, 2014-10, Vol.371 (15), p.1407-1417 [Periódico revisado por pares]Waltham, MA: Massachusetts Medical SocietyTexto completo disponível |
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4 |
Material Type: Artigo
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CTF NF1 transcription factors act as potent genetic insulators for integrating gene transfer vectorsGAUSSIN, A ; MODLICH, U ; BAUCHE, C ; NIEDERLÄNDER, N. J ; SCHAMBACH, A ; DUROS, C ; ARTUS, A ; BAUM, C ; COHEN-HAGUENAUER, O ; MERMOD, NGene therapy, 2012-01, Vol.19 (1), p.15-24 [Periódico revisado por pares]London: Nature Publishing GroupTexto completo disponível |
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5 |
Material Type: Artigo
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Improved retroviral episome transfer of transcription factors enables sustained cell fate modificationSchott, J W ; Hoffmann, D ; Maetzig, T ; Müller, F-J ; Steinemann, D ; Zychlinski, D ; Cantz, T ; Baum, C ; Schambach, AGene therapy, 2014-11, Vol.21 (11), p.938-949 [Periódico revisado por pares]England: Nature Publishing GroupTexto completo disponível |
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6 |
Material Type: Artigo
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Overcoming promoter competition in packaging cells improves production of self-inactivating retroviral vectorsSCHAMBACH, A ; MUELLER, D ; GALLA, M ; VERSTEGEN, M. M. A ; WAGEMAKER, G ; LOEW, R ; BAUM, C ; BOHNE, JGene therapy, 2006-11, Vol.13 (21), p.1524-1533 [Periódico revisado por pares]Basingstoke: Nature Publishing GroupTexto completo disponível |
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7 |
Material Type: Artigo
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Scale-up and manufacturing of clinical-grade self-inactivating γ-retroviral vectors by transient transfectionVAN DER LOO, Jcm ; SWANEY, W. P ; REEVES, L ; MALIK, P ; GRASSMAN, E ; TERWILLIGER, A ; HIGASHIMOTO, T ; SCHAMBACH, A ; BAUM, C ; THRASHER, A. J ; WILLIAMS, D. A ; NORDLING, D. LGene therapy, 2012-03, Vol.19 (3), p.246-254 [Periódico revisado por pares]London: Nature Publishing GroupTexto completo disponível |
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8 |
Material Type: Artigo
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Correction of B-cell development in Btk-deficient mice using lentiviral vectors with codon-optimized human BTKNG, Y. Y ; BAERT, M. R. M ; PIKE-OVERZET, K ; RODIJK, M ; BRUGMAN, M. H ; SCHAMBACH, A ; BAUM, C ; HENDRIKS, R. W ; VAN DONGEN, J. J. M ; STAAL, F. J. TLeukemia, 2010-09, Vol.24 (9), p.1617-1630 [Periódico revisado por pares]Avenel, NJ: Nature Publishing GroupTexto completo disponível |
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9 |
Material Type: Artigo
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Efficient in vivo regulation of cytidine deaminase expression in the haematopoietic system using a doxycycline-inducible lentiviral vector systemLachmann, N ; Brennig, S ; Pfaff, N ; Schermeier, H ; Dahlmann, J ; Phaltane, R ; Gruh, I ; Modlich, U ; Schambach, A ; Baum, C ; Moritz, TGene therapy, 2013-03, Vol.20 (3), p.298-307 [Periódico revisado por pares]England: Nature Publishing GroupTexto completo disponível |
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10 |
Material Type: Artigo
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MicroRNA-150-regulated vectors allow lymphocyte-sparing transgene expression in hematopoietic gene therapyLACHMANN, N ; JAGIELSKA, J ; MORITZ, T ; HECKL, D ; BRENNIG, S ; PFAFF, N ; MAETZIG, T ; MODLICH, U ; CANTZ, T ; GENTNER, B ; SCHAMBACH, AGene therapy, 2012-09, Vol.19 (9), p.915-924 [Periódico revisado por pares]London: Nature Publishing GroupTexto completo disponível |