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Refinado por: Base de dados/Biblioteca: Elsevier ScienceDirect Journals remover Base de dados/Biblioteca: Open Access: PubMed Central remover
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1
Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver
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Artigo
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Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver

Bell, Peter ; Moscioni, A David ; McCarter, Robert J ; Wu, Di ; Gao, Guangping ; Hoang, Albert ; Sanmiguel, Julio C ; Sun, Xun ; Wivel, Nelson A ; Raper, Steven E ; Furth, Emma E ; Batshaw, Mark L ; Wilson, James M

Molecular therapy, 2006-07, Vol.14 (1), p.34-44 [Periódico revisado por pares]

United States: Elsevier Limited

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2
What do ICU doctors do?: A multisite time and motion study of the clinical work patterns of registrars
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Artigo
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What do ICU doctors do?: A multisite time and motion study of the clinical work patterns of registrars

Li, Ling ; Hains, Isla ; Hordern, Toni ; Milliss, David ; Raper, Ray ; Westbrook, Johanna

Critical care and resuscitation, 2015-09, Vol.17 (3), p.159-166

Australia

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3
Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Adeno-associated Viral Vectors
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Artigo
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Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Adeno-associated Viral Vectors

Moscioni, David ; Morizono, Hiroki ; McCarter, Robert J ; Stern, Adam ; Cabrera-Luque, Juan ; Hoang, Albert ; Sanmiguel, Julio ; Wu, Di ; Bell, Peter ; Gao, Guang-Ping ; Raper, Steven E ; Wilson, James M ; Batshaw, Mark L

Molecular therapy, 2006-07, Vol.14 (1), p.25-33 [Periódico revisado por pares]

United States: Elsevier Limited

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4
Heterozygous variant in WNT1 gene in two brothers with early onset osteoporosis
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Artigo
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Heterozygous variant in WNT1 gene in two brothers with early onset osteoporosis

Turin, Christie G. ; Joeng, Kyu Sang ; Kallish, Staci ; Raper, Anna ; Asher, Stephanie ; Campeau, Philippe M. ; Khan, Amna N. ; Al Mukaddam, Mona

Bone Reports, 2021-12, Vol.15, p.101118, Article 101118 [Periódico revisado por pares]

Elsevier Inc

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5
Reducing Door-to-Reperfusion Time for Mechanical Thrombectomy With a Multitiered Notification System for Acute Ischemic Stroke
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Reducing Door-to-Reperfusion Time for Mechanical Thrombectomy With a Multitiered Notification System for Acute Ischemic Stroke

Goldstein, Eric D. ; Schnusenberg, Lynda ; Mooney, Lesia ; Raper, Carol C. ; McDaniel, Sheila ; Thorpe, Dallas A. ; Franke, Michelle T. ; Anderson, Linda K. ; McClure, Lynnae L. ; Oglesby, Misty M. ; Lewis, Catina Y. ; Velichko, Cammi ; Bradley, Belinda G. ; Horn, William W. ; Reid, Ashley N. ; Siegel, Jason L. ; Cannistraro, Rocco ; Bechtle, Perry ; Barbosa, Maria Thereza ; Silvers, Scott M. ; Brown, Benjamin L. ; Freeman, William D. ; Miller, David A. ; Barrett, Kevin M. ; Huang, Josephine F.

Mayo Clinic proceedings. Innovations, quality & outcomes, 2018-06, Vol.2 (2), p.119-128 [Periódico revisado por pares]

Netherlands: Elsevier Inc

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6
206. Frequency and Analysis of Liver Tumors in AAV-Treated B6C3F1 Hybrid Mice
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Artigo
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206. Frequency and Analysis of Liver Tumors in AAV-Treated B6C3F1 Hybrid Mice

Bell, Peter L. ; Moscioni, A. David ; McCarter, Robert J. ; Wu, Di ; Gao, Guang-Ping ; Hoang, Albert ; San Miguel, Julio ; Sun, Xun ; Wivel, Nelson ; Raper, Steven E. ; Furth, Emma E. ; Batshaw, Mark L. ; Wilson, James M.

Molecular therapy, 2006-05, Vol.13 (S1), p.S80-S80 [Periódico revisado por pares]

Milwaukee: Elsevier Limited

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7
De novo variants in DENND5B cause a neurodevelopmental disorder
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Artigo
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De novo variants in DENND5B cause a neurodevelopmental disorder

Scala, Marcello ; Ferla, Matteo ; Fatemi, Ali ; Phillips, John A. ; Rio, Marlene ; Siquier, Karine ; Musante, Ilaria ; Baldassari, Simona ; Iacomino, Michele ; Acosta, Maria T. ; Allworth, Aimee ; Afzali, Ben ; Bademci, Guney ; Beck, Anita ; Berry, Gerard T. ; Bican, Anna ; Bohnsack, John ; Botto, Lorenzo ; Brown, Gabrielle ; Carrasquillo, Olveen ; Chanprasert, Sirisak ; Chao, HsiaoTuan ; Chinn, Ivan ; Clark, Gary D. ; Cope, Heidi ; Craigen, William J. ; D’Souza, Precilla ; Dipple, Katrina ; Doherty, Daniel ; Doss, Argenia L. ; Fisher, Paul G. ; Fogel, Brent L. ; Gahl, William A. ; Glass, Ian ; Godfrey, Rena A. ; Grajewski, Alana ; Gropman, Andrea ; Halley, Meghan C. ; Hanchard, Neal ; Hassey, Kelly ; Hayes, Nichole ; Hom, Jason ; Huang, Alden ; Introne, Wendy ; Jarvik, Jeffrey ; Jobanputra, Vaidehi ; Kilich, Gonench ; Kohler, Jennefer N. ; Korrick, Susan ; Krasnewich, Donna M. ; Lam, Byron ; Lam, Christina ; Lanpher, Brendan C. ; Loscalzo, Joseph ; Maas, Richard L. ; Macnamara, Ellen F. ; Maduro, Valerie V. ; Marth, Gabor ; Martin, Beth A. ; Marwaha, Shruti ; McConkie-Rosell, Allyn ; McCray, Alexa T. ; Moretti, Paolo ; Morimoto, Marie ; Nakano-Okuno, Mariko ; Nieves-Rodriguez, Shirley ; Orengo, James P. ; Pace, Laura ; Parker, Neil H. ; Quinlan, Aaron ; Raper, Anna ; Reuter, Chloe M. ; Rives, Lynette ; Robertson, Amy K. ; Rodan, Lance H. ; Rossignol, Francis ; Saporta, Mario ; Schaechter, Judy ; Seto, Elaine ; Shelkowitz, Emily ; Shin, Jimann ; Solnica-Krezel, Lilianna ; Sweetser, David A. ; Sybert, Virginia ; Tarakad, Arjun ; Velinder, Matt ; Viskochil, Dave ; Ward, Patricia A. ; Wegner, Daniel ; Weisz Hubshman, Monika ; Wener, Mark ; Wenger, Tara ; Reed, Sara ; Al Saif, Hind ; Walsh, Matthew B. ; Gustincich, Stefano ; Ruggiero, Sarah M. ; Fitzgerald, Mark P. ; Helbig, Ingo ; Severino, Mariasavina

American journal of human genetics, 2024-03, Vol.111 (3), p.529-543 [Periódico revisado por pares]

United States: Elsevier Inc

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8
A syndromic neurodevelopmental disorder caused by rare variants in PPFIA3
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Artigo
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A syndromic neurodevelopmental disorder caused by rare variants in PPFIA3

Michener, Sydney L. ; Chan, Hiuling ; Rosenfeld, Jill A. ; Bekheirnia, Mir Reza ; Wagner, Matias ; Engels, Hartmut ; Guillen Sacoto, Maria J. ; McDonnell, Pamela P. ; Pastinen, Tomi ; Zhou, Dihong ; Bolton, Jeffrey ; Julia Suh, Dong Sun ; Toosi, Mehran Beiraghi ; Maroofian, Reza ; Schaefer, Gerald Bradley ; Russ-Hall, Sophie ; Carvill, Gemma L. ; Mefford, Heather ; Acosta, Maria T. ; Adams, David R. ; Amendola, Laura ; Bademci, Guney ; Balasubramanyam, Ashok ; Beck, Anita ; Bican, Anna ; Blue, Elizabeth ; Botto, Lorenzo ; Boyd, Brenna ; Briere, Lauren C. ; Brown, Gabrielle ; Carey, John ; Crouse, Andrew B. ; Dipple, Katrina ; Doss, Argenia L. ; Douine, Emilie D. ; Eckstein, David J. ; Fieg, Elizabeth L. ; Forghani, Irman ; Godfrey, Rena A. ; Grajewski, Alana ; Hahn, Sihoun ; Hisama, Fuki M. ; Hutchison, Sarah ; Introne, Wendy ; Ketkar, Shamika ; Kiley, Dana ; Kilich, Gonench ; Korrick, Susan ; Kozuira, Mary ; Krakow, Deborah ; Kravets, Elijah ; Lalani, Seema R. ; LeBlanc, Kimberly ; Levitt, Roy ; Lewis, Richard A. ; Loo, Sandra K. ; Mahoney, Rachel ; Mao, Rong ; Maravilla, Kenneth ; Marwaha, Shruti ; McCray, Alexa T. ; Mefford, Heather ; Merritt, J. Lawrence ; Morava, Eva ; Nakano-Okuno, Mariko ; Nelson, Stanley F. ; Phillips III, John A. ; Posey, Jennifer E. ; Potocki, Lorraine ; Rao, Deepak A. ; Raskind, Wendy ; Renteria, Genecee ; Reuter, Chloe M. ; Robertson, Amy K. ; Rossignol, Francis ; Ruzhnikov, Maura ; Saporta, Mario ; Seto, Elaine ; Sisco, Kathy ; Spillmann, Rebecca C. ; Stoler, Joan M. ; Tabor, Holly K. ; Tan, Queenie K.-G. ; Tan, Amelia L.M. ; Telischi, Fred ; Tifft, Cynthia J. ; Toro, Camilo ; Tran, Alyssa A. ; Ungar, Rachel A. ; Vogel, Tiphanie P. ; Wallace, Stephanie ; Wambach, Jennifer ; Wegner, Daniel ; Wener, Mark ; Wenger, Tara ; Westerfield, Monte ; Worley, Kim ; Xiao, Changrui ; Yang, John ; Chao, Hsiao-Tuan

American journal of human genetics, 2024-01, Vol.111 (1), p.96-118 [Periódico revisado por pares]

United States: Elsevier Inc

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9
Poly(Beta-Amino Ester) Nanoparticles Enable Nonviral Delivery of CRISPR-Cas9 Plasmids for Gene Knockout and Gene Deletion
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Poly(Beta-Amino Ester) Nanoparticles Enable Nonviral Delivery of CRISPR-Cas9 Plasmids for Gene Knockout and Gene Deletion

Rui, Yuan ; Varanasi, Mahita ; Mendes, Shanelle ; Yamagata, Hannah M. ; Wilson, David R. ; Green, Jordan J.

Molecular therapy. Nucleic acids, 2020-06, Vol.20, p.661-672 [Periódico revisado por pares]

United States: Elsevier Inc

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10
A Phase I Trial of Intravenous CG7870, a Replication-Selective, Prostate-Specific Antigen-Targeted Oncolytic Adenovirus, for the Treatment of Hormone-Refractory, Metastatic Prostate Cancer
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A Phase I Trial of Intravenous CG7870, a Replication-Selective, Prostate-Specific Antigen-Targeted Oncolytic Adenovirus, for the Treatment of Hormone-Refractory, Metastatic Prostate Cancer

Small, Eric J ; Carducci, Michael A ; Burke, James M ; Rodriguez, Ron ; Fong, Lawrence ; van Ummersen, Lynn ; Yu, D C ; Aimi, Junko ; Ando, Dale ; Working, Peter ; Kirn, David ; Wilding, George

Molecular therapy, 2006-07, Vol.14 (1), p.107-117 [Periódico revisado por pares]

United States: Elsevier Limited

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