PP09.16 – 2691: Eteplirsen, a phosphorodiamidate morpholino oligomer (PMO) for the treatment of Duchenne muscular dystrophy (DMD): 3.2 year update on six-minute walk test (6MWT), pulmonary function testing (PFT), and safety
Kaye, E.M ; Mendell, J.R ; Rodino-Klapac, L ; Sahenk, Z ; Roush, K ; Lowes, L.P ; Alfano, L ; Gomez, A.M ; Malik, V ; Flanigan, K.M ; Shilling, C ; Duda, P ; Saoud, J
European journal of paediatric neurology, 2015-05, Vol.19, p.S69-S69 [Periódico revisado por pares]Elsevier Ltd
Texto completo disponível