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The effect of enzyme replacement therapy on clinical outcomes in male patients with Fabry disease: A systematic literature review by a European panel of experts

Germain, Dominique P. ; Elliott, Perry M. ; Falissard, Bruno ; Fomin, Victor V. ; Hilz, Max J. ; Jovanovic, Ana ; Kantola, Ilkka ; Linhart, Aleš ; Mignani, Renzo ; Namdar, Mehdi ; Nowak, Albina ; Oliveira, João-Paulo ; Pieroni, Maurizio ; Viana-Baptista, Miguel ; Wanner, Christoph ; Spada, Marco

Molecular genetics and metabolism reports, 2019-06, Vol.19, p.100454-100454, Article 100454 [Periódico revisado por pares]

United States: Elsevier Inc

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