Successful RAG1-SCID gene therapy depends on the level of RAG1 expression
Pike-Overzet, Karin, PhD ; Baum, Christopher, MD ; Bredius, Robbert G.M., MD, PhD ; Cavazzana, Marina, MD, PhD ; Driessen, Gert-Jan, MD, PhD ; Fibbe, Willem E., MD, PhD ; Gaspar, H. Bobby, MD, PhD ; Hoeben, Rob C., PhD ; Lagresle-Peyrou, Chantal, PhD ; Lankester, Arjan, MD, PhD ; Meij, Pauline, PhD ; Schambach, Axel, MD, PhD ; Thrasher, Adrian, MD, PhD ; Van Dongen, Jacques J.M., MD, PhD ; Zwaginga, Jaap-Jan, MD, PhD ; Staal, Frank J.T., PhD
Journal of allergy and clinical immunology, 2014-07, Vol.134 (1), p.242-243 [Periódico revisado por pares]United States: Elsevier Inc
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