Mechanism of action and therapeutic route for a muscular dystrophy caused by a genetic defect in lipid metabolism
Tavasoli, Mahtab ; Lahire, Sarah ; Sokolenko, Stanislav ; Novorolsky, Robyn ; Reid, Sarah Anne ; Lefsay, Abir ; Otley, Meredith O C ; Uaesoontrachoon, Kitipong ; Rowsell, Joyce ; Srinivassane, Sadish ; Praest, Molly ; MacKinnon, Alexandra ; Mammoliti, Melissa Stella ; Maloney, Ashley Alyssa ; Moraca, Marina ; Pedro Fernandez-Murray, J ; McKenna, Meagan ; Sinal, Christopher J ; Nagaraju, Kanneboyina ; Robertson, George S ; Hoffman, Eric P ; McMaster, Christopher R
Nature communications, 2022-03, Vol.13 (1), p.1559-1559, Article 1559 [Periódico revisado por pares]England: Nature Publishing Group
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