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Preexisting Immunity and Low Expression in Primates Highlight Translational Challenges for Liver-directed AAV8-mediated Gene Therapy

Hurlbut, Gregory D ; Ziegler, Robin J ; Nietupski, Jennifer B ; Foley, Joseph W ; Woodworth, Lisa A ; Meyers, Elizabeth ; Bercury, Scott D ; Pande, Nilesh N ; Souza, David W ; Bree, Mark P ; Lukason, Michael J ; Marshall, John ; Cheng, Seng H ; Scheule, Ronald K

Molecular therapy, 2010-11, Vol.18 (11), p.1983-1994 [Periódico revisado por pares]

United States: Elsevier Inc

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