CRISPR-Cas9 base editing of pathogenic CaMKII[delta] improves cardiac function in a humanized mouse model

Lebek, Simon ; Caravia, Xurde M ; Straub, Leon G ; Alzhanov, Damir ; Tan, Wei ; Li, Hui ; McAnally, John R ; Chen, Kenian ; Xu, Lin ; Scherer, Philipp E ; Liu, Ning ; Bassel-Duby, Rhonda ; Olson, Eric N

The Journal of clinical investigation, 2024-01, Vol.134 (1) [Periódico revisado por pares]

American Society for Clinical Investigation

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